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WhatIsLCA
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LCA7

CRX

Cone-rod homeobox transcription factor; critical for photoreceptor differentiation

No Targeted Treatment Yet

Chromosomal Locus

19q13.33

Inheritance

Autosomal Dominant

Frequency

~1% of LCA cases

OMIM #613829

Key Clinical Features

  • 1Extensive clinical heterogeneity (including intrafamilial variability)
  • 2Macular degeneration most prominent
  • 3Can be autosomal dominant

Sources: